Day One - Wednesday August 20

8:55 am Chair’s Opening Remarks

Driving for Better Patient Experience Throughout Patient Journey to Optimize for Patient Retention

9:00 am Maximizing Patient Education & Collaboration During Research & Development to Support Patient Preparation to Receive a Therapy

Synopsis

  • Educating patients on the science, risks, and benefits of cell or gene therapies to guide patients to a well-informed decision
  • Fostering transparent conversations to involve patients in clinical trial design and treatment decisions
  • Highlighting the role of patient feedback to shape ethical and accessible R&D pathways

9:30 am Optimizing Healthcare Readiness & Treatment Experiences to Assist Patients Throughout Treatment Journey

  • Rohita Sharma Senior Director - Global Strategic Alliances, Patient Experience, Medical Affairs, Patient Insights, Solutions & Rare Diseases, Alexion Pharmaceuticals

Synopsis

  • Addressing patient concerns and maintaining open communication during treatment to support patients through their challenges
  • Revealing system gaps in healthcare stakeholders like payers and healthcare professionals to establish sustainable adoption of a therapy
  • Developing innovative access models to ensure affordability and equitable delivery of therapies

10:00 am Morning Refreshment Break & Speed Networking

Utilizing Patient Involvement to Achieve Regulatory Approval

11:00 am Roundtable Discussion: Educating Patients on the Next Steps Following the Current US Health Agency Layoffs to Manage Patient Expectations

Synopsis

  • Addressing the current layoffs occurring at agencies of the Health and Human Services like the FDA to introduce regulatory challenges
  • Predicting the potential patient engagement issues this will cause to prepare biopharma and patient groups for new solutions
  • Developing strategies to inform patients on the current issues to manage patients understanding and expectations

12:00 pm Lunch Break and Networking

1:15 pm Discussion Session: Debating Whether Patient Organization Leaders Should be Involved in Regulatory Meetings to Optimize Patient Transparency

  • Pat Furlong Founding President & Chief Executive Officer, Parent Project Muscular Dystrophy
  • Marcelyne Joseney-Antoine Clinical Operations & Hematology Asset Lead, Beam Therapeutics

Synopsis

  • Comparing different views of early patient groups implementation during regulatory meetings to utilize patient voices
  • Assessing the risks and benefits of early patient implementation to evaluate its necessity
  • Reviewing the process of how patient insights are passed to regulatory bodies to ensure clear translation of patients’ needs

2:15 pm Afternoon Break & Networking

Exploring the Innovative Methods of Cell & Gene Therapy Education to Improve Patient Awareness

2:45 pm Case Study: Demonstrating New Digital Education Tools for CAR-T to Support Shared Decision Making in Cell Therapy

  • Amy Corrao Senior Director, US & Worldwide Portfolio Strategy, Cell Therapy, Bristol Myers Squibb

Synopsis

  • Exploring the different challenges of educating CAR-T to optimize for improved CAR-T specific educational material
  • Showcase the recurring challenges faced by prevalent diseases group throughout a CAR-T lifecycle to improve CAR-T specific patient centricity
  • Outline the real time methods used to overcome challenges to ensure clear and transparent interaction of patient groups

3:15 pm Understanding the Differences Between Prevalent & Rare Diseases to Optimize Tailored Patient Educational Materials

Synopsis

  • Contrasting the challenges of prevalent and rare diseases to validate potential educational approaches for each disease type.
  • Learning new methodologies of creating educational materials to optimize patient transparency
  • Addressing cell and gene specific patient insights to improve patient education materials

4:00 pm End of Conference Day One